... However, it’s still a complex procedure and is only used for certain PI conditions.In the United States, the FDA has approved gene therapies for some primary immunodeficiency disorders, including etuvetidigene autotemcel (Waskyra) for Wiskott-Aldrich syndrome and marnetegragene autotemcel (Kresladi) for severe leukocyte adhesion deficiency type 1.For ...
7 Treatment Options for Primary Immunodeficiency
... However, it’s still a complex procedure and is only used for certain PI conditions.In the United States, the FDA has approved gene therapies for some primary immunodeficiency disorders, including etuvetidigene autotemcel (Waskyra) for Wiskott-Aldrich syndrome and marnetegragene autotemcel (Kresladi) for severe leukocyte adhesion deficiency type 1.For ...